CRISPR/Cas9 can reverse multiple diseases in mice

New use for the genetic tool turns genes on instead of snipping them

mouse muscle fibers

PUMP IT UP  A new type of CRISPR/Cas9-based gene therapy turned on muscle-building genes in mice that have muscular dystrophy. Muscle fibers (magenta) from mice that got the therapy (right) were bigger than fibers from untreated animals (left).

H.-K. Liao et al/Cell 2017

A new twist on gene editing makes the CRISPR/Cas9 molecular scissors act as a highlighter for the genetic instruction book.